The Independent on MSN

Boy diagnosed with SMA after symptoms dismissed as 'totally normal'

Boy diagnosed with SMA after first symptoms dismissed as ‘totally normal’ - Sid was diagnosed with spinal muscular atrophy ...

'I want to tell Jesy Nelson, there's hope', says mum of child with SMA

A County Armagh mother, whose five-year-old daughter has Spinal Muscular Atrophy (SMA), has said singer Jesy Nelson should ...
The American Journal of Managed Care

Innovations in SMA Treatment: The Last Decade and Beyond

The recent availability of 3 FDA-approved treatments for patients with spinal muscular atrophy (SMA) has dramatically altered patient outcomes and provided a wealth of new avenues for SMA ...
Science Daily

New target found for treatment of spinal muscular atrophy

Medical researchers have uncovered a novel mechanism that leads to motor neuron degeneration in spinal muscular atrophy (SMA). This discovery offers a new target for treatment that overcomes ...
Arabian Business

Medcare delivers gene therapy treatment for first international SMA patient

The newly licensed intrathecal gene therapy expands life-changing treatment options for children and adults affected by ...
The American Journal of Managed Care

Shared Decision-Making Is Essential Prior to SMA-Enhancing Treatments

Shared decision-making between patients and healthcare providers is essential for optimal SMA treatment outcomes and quality of life. Early treatment initiation is crucial for infants, while older ...