Cold Spring Harbor Laboratory researchers have reported that a bespoke antisense oligonucleotide can disrupt alternative ...

Program to feature presentations from the company management about KRRO-121 for the potential treatment of hyperammonemia, a leading clinical hepatologist about ammonia-driven diseases, and a caregive ...

The global oligonucleotide CDMO market is poised for growth driven by the rising clinical pipeline of RNA-based therapies, ...

Researchers from Carnegie Mellon University have discovered a way to target RNA that could lead to new treatment options for ...

For the first time, a drug to treat adult patients with familial chylomicronemia syndrome (FCS), a severe and rare condition that leads to extremely high levels of blood fats called triglycerides, has ...

Researchers from Carnegie Mellon University have discovered a way to target RNA that could lead to new treatment options for myotonic dystrophy type 1 (DM1), the most common adult-onset form of ...

Elevated levels of lipoprotein (a) is a genetic disease that causes cardiovascular disease. Steven Nissen, M.D., addresses why it’s important to find treatments for this genetic risk factor.

Department of Surgery, University of California Los Angeles, Los Angeles, United States The final, formatted version of the article will be published soon. Background/Objectives: Schizophrenia is a ...